Clinical Trials Directory

Trials / Conditions / Inherited Metabolic Disorders (IMD)

Inherited Metabolic Disorders (IMD)

5 registered clinical trials studyying Inherited Metabolic Disorders (IMD)2 currently recruiting.

StatusTrialSponsorPhase
RecruitingData Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
NCT04528355
Paul Szabolcs
TerminatedA Follow-up Study in Patients With Inherited Metabolic Disorders (IMD) Who Underwent Hematopoietic Stem Cell T
NCT04008849
Magenta Therapeutics, Inc.
CompletedMGTA-456 in Patients With Inherited Metabolic Disorders Undergoing Hematopoietic Stem Cell Transplantation (HS
NCT03406962
Magenta Therapeutics, Inc.Phase 2
WithdrawnSafety and Exploratory Efficacy of HSC835 in Patients With Inherited Metabolic Disorders (IMD)
NCT02715505
Novartis PharmaceuticalsPhase 1 / Phase 2
RecruitingReduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
NCT01962415
Paul SzabolcsPhase 2