Clinical Trials Directory

Trials / Conditions / Heredodegenerative Disorders, Nervous System

Heredodegenerative Disorders, Nervous System

3 registered clinical trials studyying Heredodegenerative Disorders, Nervous System.

StatusTrialSponsorPhase
CompletedExtension of AOC 1001-CS1 (MARINA) Study in Adult Myotonic Dystrophy Type 1 (DM1) Patients
NCT05479981
Avidity Biosciences, Inc.Phase 2
WithdrawnMitogen Activated Protein Kinase Kinase (MEK1/2) Inhibitor Selumetinib (AZD6244 Hydrogen Sulfate) in People Wi
NCT03109301
National Cancer Institute (NCI)Phase 2
CompletedAn Analysis of the Symptomatic Domains Most Relevant to Charcot Marie Tooth Neuropathy (CMT) Patients
NCT02429947
University of South Florida