Clinical Trials Directory

Trials / Conditions / Hereditary Inclusion Body Myopathy (HIBM)

Hereditary Inclusion Body Myopathy (HIBM)

4 registered clinical trials studyying Hereditary Inclusion Body Myopathy (HIBM).

StatusTrialSponsorPhase
CompletedEfficacy Confirmation Study of NPC-09
NCT04671472
NobelpharmaPhase 3
CompletedAn Open Label Phase 2 Extension Study of Higher Dose Sialic Acid-Extended Release (SA-ER) Tablets and Sialic A
NCT01830972
Ultragenyx Pharmaceutical IncPhase 2
CompletedPhase I Clinical Trial of ManNAc in Patients With GNE Myopathy or Hereditary Inclusion Body Myopathy (HIBM)
NCT01634750
National Human Genome Research Institute (NHGRI)Phase 1
CompletedSafety and Pharmacokinetics of Sialic Acid Tables in Patients With Hereditary Inclusion Body Myopathy (HIBM)
NCT01359319
Ultragenyx Pharmaceutical IncPhase 1