Trials / Conditions / Hereditary Inclusion Body Myopathy

Hereditary Inclusion Body Myopathy

8 registered clinical trials studyying Hereditary Inclusion Body Myopathy.

Status	Trial	Sponsor	Phase
Terminated	Study to Evaluate the Safety and Efficacy of Aceneuramic Acid Extended-Release (Ace-ER) Tablets in Patients Wi NCT02736188	Ultragenyx Pharmaceutical Inc	Phase 3
Terminated	A Study to Evaluate the Safety of Aceneuramic Acid Extended Release (Ace-ER; UX001) Tablets in Glucosamine (UD NCT02731690	Ultragenyx Pharmaceutical Inc	Phase 2
Completed	Phase 3 Randomized, Double-Blind, Placebo-Controlled Study to Evaluate Sialic Acid in Patients With Glucosamin NCT02377921	Ultragenyx Pharmaceutical Inc	Phase 3
Unknown	International GNE Myopathy Patient Registry NCT04009226	Newcastle University	—
Completed	GNE-Myopathy Disease Monitoring Program (GNEM-DMP): A Registry and Prospective Observational Natural History S NCT01784679	Ultragenyx Pharmaceutical Inc	—
Completed	A Phase 2 Study to Evaluate the Dose and Pharmacodynamic Efficacy of Sialic Acid-Extended Release (SA-ER) Tabl NCT01517880	Ultragenyx Pharmaceutical Inc	Phase 2
Completed	Pharmacokinetic Study on N-acetylneuraminic Acid NCT01236898	Tohoku University	Phase 1
Completed	Intravenous Immune Globulin to Treat Hereditary Inclusion Body Myopathy NCT00195637	National Human Genome Research Institute (NHGRI)	Phase 1