Clinical Trials Directory

Trials / Conditions / Glycogen Storage Disease Type IA

Glycogen Storage Disease Type IA

11 registered clinical trials studyying Glycogen Storage Disease Type IA — 4 currently recruiting.

StatusTrialSponsorPhase
RecruitingAccuracy of Home Lactate Meter and Accu-chek Glucometer in Patients With Glycogen Storage Disease
NCT07459582
Connecticut Children's Medical Center—
RecruitingAccuracy of Lactate Meter in GSDIa
NCT06843330
Connecticut Children's Medical Center—
RecruitingA Phase 1/2, Dose-Exploration Study to Evaluate the Safety and Efficacy of BEAM-301 in Patients With Glycogen
NCT06735755
Beam Therapeutics Inc.Phase 1 / Phase 2
RecruitingGlycogen Storage Disease Type Ia (GSDIa) Disease Monitoring Program
NCT06636383
Ultragenyx Pharmaceutical Inc—
CompletedA Study of Adeno-Associated Virus Serotype 8-Mediated Gene Transfer of Glucose-6-Phosphatase in Patients With
NCT05139316
Ultragenyx Pharmaceutical IncPhase 3
TerminatedAdeno-Associated Virus (AAV) Antibody Study in Subjects OTC Deficiency, GSDIa, and Wilson Disease
NCT04909346
Ultragenyx Pharmaceutical Inc—
CompletedEndogenous Glucose Production in Patients With Glycogen Storage Disease Type Ia
NCT04311307
University Medical Center GroningenPhase 1 / Phase 2
CompletedRetrospective Study of Glucose Monitoring for Glycemic Control in Patients With GSDIa
NCT04708015
Ultragenyx Pharmaceutical Inc—
CompletedStudy of Long-Term Safety and Efficacy on Gene Therapy in Glycogen Storage Disease Type Ia
NCT03970278
Ultragenyx Pharmaceutical Inc—
CompletedSleep and Quality of Life in Patients With Glycogen Storage Disease on Standard Versus Modified Uncooked Corns
NCT02054832
John Mitchell—
CompletedStudy of the Relationship Between Glycogen Storage Disease Type Ia and Inflammatory Bowel Disease
NCT01854242
University of Florida—