Trials / Conditions / Fanconi Anemia Complementation Group A
Fanconi Anemia Complementation Group A
4 registered clinical trials studyying Fanconi Anemia Complementation Group A.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Active Not Recruiting | Gene Therapy for Fanconi Anemia, Complementation Group A NCT04248439 | Rocket Pharmaceuticals Inc. | Phase 2 |
| Active Not Recruiting | Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy NCT04437771 | Rocket Pharmaceuticals Inc. | — |
| Active Not Recruiting | Lentiviral-mediated Gene Therapy for Pediatric Patients With Fanconi Anemia Subtype A NCT04069533 | Rocket Pharmaceuticals Inc. | Phase 2 |
| Unknown | A Clinical Trial to Evaluate the Safety of RP-L102 in Pediatric Subjects With Fanconi Anemia Subtype A NCT03814408 | Rocket Pharmaceuticals Inc. | Phase 1 |