Clinical Trials Directory

Trials / Conditions / Distal Myopathy With Rimmed Vacuoles

Distal Myopathy With Rimmed Vacuoles

3 registered clinical trials studyying Distal Myopathy With Rimmed Vacuoles.

StatusTrialSponsorPhase
TerminatedStudy to Evaluate the Safety and Efficacy of Aceneuramic Acid Extended-Release (Ace-ER) Tablets in Patients Wi
NCT02736188
Ultragenyx Pharmaceutical IncPhase 3
TerminatedA Study to Evaluate the Safety of Aceneuramic Acid Extended Release (Ace-ER; UX001) Tablets in Glucosamine (UD
NCT02731690
Ultragenyx Pharmaceutical IncPhase 2
CompletedPhase 3 Randomized, Double-Blind, Placebo-Controlled Study to Evaluate Sialic Acid in Patients With Glucosamin
NCT02377921
Ultragenyx Pharmaceutical IncPhase 3