Clinical Trials Directory

Trials / Conditions / Danon Disease

Danon Disease

7 registered clinical trials studyying Danon Disease4 currently recruiting.

StatusTrialSponsorPhase
RecruitingRare Glycogen Storage Diseases Natural History Study
NCT06795152
Duke University
RecruitingDanon Disease Natural History Study
NCT06214507
Rocket Pharmaceuticals Inc.
RecruitingA Gene Therapy Study of RP-A501 in Male Patients With Danon Disease
NCT06092034
Rocket Pharmaceuticals Inc.Phase 2
CompletedNatural History of Danon Disease
NCT05548855
Rocket Pharmaceuticals Inc.
UnknownGene Therapy for Male Patients With Danon Disease (DD) Using RP-A501; AAV9.LAMP2B
NCT03882437
Rocket Pharmaceuticals Inc.Phase 1
UnknownThe Natural History of Danon Disease
NCT03766386
University of California, San Diego
RecruitingPrecision Diagnosis and Risk Stratification of Rare Cardiomyopathies Based on Novel Cardiac Magnetic Resonance
NCT07336394
Chinese Academy of Medical Sciences, Fuwai Hospital