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Trials / Conditions / Creatine Deficiency, X-linked

Creatine Deficiency, X-linked

3 registered clinical trials studyying Creatine Deficiency, X-linked1 currently recruiting.

StatusTrialSponsorPhase
UnknownOptical Imaging as a Tool for Monitoring Brain Function in Creatine Deficiency Syndromes
NCT06292884
IRCCS Fondazione Stella Maris
RecruitingWeb Intervention for Parents of Youth With Genetic Syndromes (WINGS)
NCT06139172
Rush University Medical CenterN/A
TerminatedObservational Study of Males With Creatine Transporter Deficiency
NCT02931682
Ultragenyx Pharmaceutical Inc