Clinical Trials Directory

Trials / Conditions / Congenital Myotonic Dystrophy

Congenital Myotonic Dystrophy

8 registered clinical trials studyying Congenital Myotonic Dystrophy5 currently recruiting.

StatusTrialSponsorPhase
RecruitingTrial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension
NCT06747884
Virginia Commonwealth University
RecruitingDMCRN-02-001: Assessing Pediatric Endpoints in DM1
NCT05224778
Virginia Commonwealth University
RecruitingSafety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy
NCT05004129
AMO Pharma LimitedPhase 2 / Phase 3
CompletedEfficacy and Safety of Tideglusib in Congenital Myotonic Dystrophy
NCT03692312
AMO Pharma LimitedPhase 2 / Phase 3
CompletedTrial Readiness and Endpoint Assessment in Congenital Myotonic Dystrophy
NCT03059264
Virginia Commonwealth University
RecruitingMyotonic Dystrophy Family Registry
NCT02398786
Myotonic Dystrophy Foundation
RecruitingMyotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
NCT00082108
University of Rochester
AvailableTideglusib: Expanded Access Use in Congenital Myotonic Dystrophy
NCT07119775
AMO Pharma Limited