Trials / Conditions / Congenital Muscular Dystrophy
Congenital Muscular Dystrophy
6 registered clinical trials studyying Congenital Muscular Dystrophy — 2 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Recruiting | Assessments in Patients With Muscular Pathology and in Control Subjects : The ActiLiège Next Study NCT05982119 | Centre Hospitalier Universitaire de Liege | N/A |
| Recruiting | Swiss Registry for Neuromuscular Disorders NCT05102916 | University of Bern | — |
| Completed | Congenital Muscular Dystrophy Ascending Multiple Dose Cohort Study Analyzing Pharmacokinetics at Three Dose Le NCT01805024 | Santhera Pharmaceuticals | Phase 1 |
| Unknown | Global FKRP Registry NCT04001595 | Newcastle University | — |
| Completed | A Study to Test Lung Stretch Therapy (Hyperinsufflation) in Children With Collagen VI Muscular Dystrophy NCT01836627 | Children's Hospital Medical Center, Cincinnati | N/A |
| Completed | Flu Vaccine Study in Neuromuscular Patients 2011 NCT01422200 | Children's Hospital Medical Center, Cincinnati | Phase 4 |