Trials / Conditions / CFTR Gene Mutation
CFTR Gene Mutation
3 registered clinical trials studyying CFTR Gene Mutation — 2 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Recruiting | Safety, Tolerability and Efficacy Study of ARCT-032 in People With Cystic Fibrosis NCT06747858 | Arcturus Therapeutics, Inc. | Phase 2 |
| Recruiting | Cystic Fibrosis in the Kidney: Monitoring the Effectiveness of Elexacaftor/tezacaftor/ivacaftor in Urine After NCT05818319 | University of Aarhus | N/A |
| Terminated | Validation of Therapeutic Efficacy Targeting the Splicing Variants in Cystic Fibrosis and CFTR Pathologies NCT05100823 | University Hospital, Montpellier | N/A |