Clinical Trials Directory

Trials / Conditions / Canavan Disease

Canavan Disease

11 registered clinical trials studyying Canavan Disease — 4 currently recruiting.

StatusTrialSponsorPhase
RecruitingA Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)
NCT04998396
Aspa TherapeuticsPhase 1 / Phase 2
Enrolling By InvitationrAAV-Olig001-ASPA Gene Therapy for Treatment of Children With Typical Canavan Disease
NCT04833907
Myrtelle Inc.Phase 1 / Phase 2
CompletedNatural History Study of Patients With Canavan Disease (CANinform Study)
NCT04126005
Aspa Therapeutics—
Enrolling By InvitationEarly Check: Expanded Screening in Newborns
NCT03655223
RTI International—
CompletedLeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for Leukodystrophies
NCT02699190
Children's Hospital of Philadelphia—
RecruitingThe Myelin Disorders Biorepository Project
NCT03047369
Children's Hospital of Philadelphia—
CompletedA Natural History Study of Canavan Disease
NCT02851563
NYU Langone Health—
CompletedEfficacy Study of an Online Educational Module Before Carrier Genetic Screening in Persons of Ashkenazi Jewish
NCT01999257
McGill University Health Centre/Research Institute of the McGill University Health CentreN/A
WithdrawnLithium and Acetate for Canavan Disease
NCT00657748
Assistance Publique - Hôpitaux de ParisPhase 2
UnknownOral Glyceryl Triacetate (GTA) in Newborns With Canavan
NCT00724802
Shaare Zedek Medical CenterN/A
No Longer AvailableCanavan-Single Patient IND
NCT05317780
University of Florida—