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Trials / Conditions / Brain Diseases, Metabolic, Inborn

Brain Diseases, Metabolic, Inborn

4 registered clinical trials studyying Brain Diseases, Metabolic, Inborn3 currently recruiting.

StatusTrialSponsorPhase
RecruitingEffect of Large Neutral Amino Acids in Adults With Classical Phenylketonuria
NCT06337864
Rigshospitalet, DenmarkN/A
RecruitingUCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-
NCT02254863
Joanne Kurtzberg, MDPhase 1
CompletedNeurologic Injuries in Adults With Urea Cycle Disorders
NCT00472732
Andrea Gropman
RecruitingLongitudinal Study of Urea Cycle Disorders
NCT00237315
Andrea Gropman