Trials / Conditions / ATP-Binding Cassette Subfamily C Member 6 Deficiency
ATP-Binding Cassette Subfamily C Member 6 Deficiency
4 registered clinical trials studyying ATP-Binding Cassette Subfamily C Member 6 Deficiency — 2 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Recruiting | PROPEL - A Prospective Observational Patient Registry to Evaluate ENPP1 and ABCC6 Deficiency NCT06302439 | Inozyme Pharma | — |
| Recruiting | The ENERGY Study: Evaluation of Safety and Tolerability of INZ-701 in Infants With ENPP1 Deficiency or ABCC6 D NCT05734196 | Inozyme Pharma | Phase 1 |
| Completed | Natural History Study of ENPP1 Deficiency and the Early-onset Form of ABCC6 Deficiency NCT05050669 | Inozyme Pharma | — |
| Completed | Evaluation of Safety, Tolerability, and Efficacy of INZ-701 in Adults With ABCC6 Deficiency Causing PXE NCT05030831 | Inozyme Pharma | Phase 1 / Phase 2 |