Clinical Trials Directory

Trials / Conditions / Amyloidosis, Hereditary, Transthyretin-Related

Amyloidosis, Hereditary, Transthyretin-Related

6 registered clinical trials studyying Amyloidosis, Hereditary, Transthyretin-Related2 currently recruiting.

StatusTrialSponsorPhase
Not Yet RecruitingTo Evaluate the Long-term Safety and Tolerability of Acoramidis in Participants With Newly Diagnosed ATTR-CM (
NCT07116473
Eidos Therapeutics, a BridgeBio companyPhase 3
RecruitingExercise in Hereditary ATTR (ATTRv) Amyloidosis
NCT07033715
University of MaiaN/A
UnknownAnalysis of the Instestinal Microbiome of Patients With Transthyretin Amyloidosis
NCT05196594
University of Sao Paulo General Hospital
CompletedENDEAVOUR: Phase 3 Multicenter Study of Revusiran (ALN-TTRSC) in Patients With Transthyretin (TTR) Mediated Fa
NCT02319005
Alnylam PharmaceuticalsPhase 3
CompletedAPOLLO: The Study of an Investigational Drug, Patisiran (ALN-TTR02), for the Treatment of Transthyretin (TTR)-
NCT01960348
Alnylam PharmaceuticalsPhase 3
Approved For MarketingExpanded Access Protocol of Patisiran for Patients With Hereditary ATTR Amyloidosis (hATTR)
NCT02939820
Alnylam Pharmaceuticals