Trials / Conditions / Amyloidosis, Familial
Amyloidosis, Familial
5 registered clinical trials studyying Amyloidosis, Familial — 4 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Not Yet Recruiting | To Evaluate the Long-term Safety and Tolerability of Acoramidis in Participants With Newly Diagnosed ATTR-CM ( NCT07116473 | Eidos Therapeutics, a BridgeBio company | Phase 3 |
| Recruiting | Comprehensive Program for Hereditary Transthyretin Amyloidosis NCT07213297 | Hospital de Alta Complejidad en Red | — |
| Recruiting | A Phase 3 Study of NTLA-2001 in ATTRv-PN NCT06672237 | Intellia Therapeutics | Phase 3 |
| Recruiting | Subclinical Transthyretin Cardiac Amyloidosis in V122I TTR Carriers NCT05489549 | University of Texas Southwestern Medical Center | — |
| Completed | Patisiran in Patients With Hereditary Transthyretin-mediated Amyloidosis (hATTR Amyloidosis) Disease Progressi NCT03862807 | Alnylam Pharmaceuticals | Phase 3 |