Clinical Trials Directory

Trials / Conditions / Amyloid Neuropathies, Familial

Amyloid Neuropathies, Familial

6 registered clinical trials studyying Amyloid Neuropathies, Familial1 currently recruiting.

StatusTrialSponsorPhase
RecruitingA Phase 3 Study of NTLA-2001 in ATTRv-PN
NCT06672237
Intellia TherapeuticsPhase 3
CompletedEarly and Systematic Screening in Chronic Neuropathy
NCT03720275
University Hospital, BordeauxN/A
CompletedMonitoring of Early Disease Progression in Hereditary Transthyretin Amyloidosis
NCT03431896
The Cleveland Clinic
CompletedENDEAVOUR: Phase 3 Multicenter Study of Revusiran (ALN-TTRSC) in Patients With Transthyretin (TTR) Mediated Fa
NCT02319005
Alnylam PharmaceuticalsPhase 3
CompletedAPOLLO: The Study of an Investigational Drug, Patisiran (ALN-TTR02), for the Treatment of Transthyretin (TTR)-
NCT01960348
Alnylam PharmaceuticalsPhase 3
Approved For MarketingExpanded Access Protocol of Patisiran for Patients With Hereditary ATTR Amyloidosis (hATTR)
NCT02939820
Alnylam Pharmaceuticals