Clinical Trials Directory

Trials / Conditions / Amino Acid Metabolism, Inborn Errors

Amino Acid Metabolism, Inborn Errors

6 registered clinical trials studyying Amino Acid Metabolism, Inborn Errors2 currently recruiting.

StatusTrialSponsorPhase
RecruitingEffect of Large Neutral Amino Acids in Adults With Classical Phenylketonuria
NCT06337864
Rigshospitalet, DenmarkN/A
TerminatedAtaluren for Nonsense Mutation Methylmalonic Acidemia
NCT01141075
PTC TherapeuticsPhase 2
CompletedArginine and Buphenyl in Patients With Argininosuccinic Aciduria (ASA), a Urea Cycle Disorder
NCT00345605
Brendan LeePhase 2
RecruitingLongitudinal Study of Urea Cycle Disorders
NCT00237315
Andrea Gropman
UnknownStudy of Treatment and Metabolism in Patients With Urea Cycle Disorders
NCT00004307
National Center for Research Resources (NCRR)Phase 1
CompletedPhase II Study of Sodium Phenylbutyrate, Sodium Benzoate, Sodium Phenylacetate, and Dietary Intervention for U
NCT00004767
National Center for Research Resources (NCRR)Phase 2