Clinical Trials Directory

Trials / Conditions / Allan-Herndon-Dudley Syndrome

Allan-Herndon-Dudley Syndrome

9 registered clinical trials studyying Allan-Herndon-Dudley Syndrome3 currently recruiting.

StatusTrialSponsorPhase
CompletedWithdrawal of Tiratricol Treatment in Males With Monocarboxylate Transporter 8 Deficiency (MCT8 Deficiency)
NCT05579327
Rare Thyroid Therapeutics International ABPhase 3
CompletedMCT8 Deficiency Caregiver Study
NCT06060197
Rare Thyroid Therapeutics International AB
RecruitingRegister for Patients With Thyroid Hormone Resistance.
NCT06566066
Charite University, Berlin, Germany
Active Not RecruitingTriac Trial II in MCT8 Deficiency Patients
NCT02396459
Rare Thyroid Therapeutics International ABPhase 2
RecruitingGROWing Up With Rare GENEtic Syndromes
NCT04463316
dr. Laura C. G. de Graaff-Herder
CompletedLeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for Leukodystrophies
NCT02699190
Children's Hospital of Philadelphia
RecruitingThe Myelin Disorders Biorepository Project
NCT03047369
Children's Hospital of Philadelphia
CompletedThyroid Hormone Analog Therapy in MCT8 Deficiency: Triac Trial Patients
NCT02060474
Erasmus Medical CenterPhase 2
AvailableExpanded Access Program for Tiratricol in Patients With Monocarboxylate Transporter 8 Deficiency
NCT05911399
Rare Thyroid Therapeutics International AB