Trials / Conditions / Alexander Disease
Alexander Disease
5 registered clinical trials studyying Alexander Disease — 2 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Active Not Recruiting | A Study to Evaluate the Safety and Efficacy of Zilganersen (ION373) in Patients With Alexander Disease (AxD) NCT04849741 | Ionis Pharmaceuticals, Inc. | Phase 3 |
| Completed | LeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for Leukodystrophies NCT02699190 | Children's Hospital of Philadelphia | — |
| Recruiting | The Myelin Disorders Biorepository Project NCT03047369 | Children's Hospital of Philadelphia | — |
| Recruiting | Evaluation of Outcome Metrics in Alexander Disease NCT02714764 | Children's Hospital of Philadelphia | — |
| Available | Zilganersen Expanded Access Program for Individuals With Alexander Disease NCT07487389 | Ionis Pharmaceuticals, Inc. | — |